according to researchers from the Italian Medicines Agency (AIFA). “It is a quite high number,” Fabrizio Gianfrate, a professor of health economics at the University of Ferrara who was not ...

AIFA, the Italian Medicines Agency and the agency tasked with both pricing and reimbursement of medicines in Italy, published a consultation on their guidance on criteria and methods for pricing ...

Fondazione Telethon, an Italian biomedical charity focused on rare genetic diseases, has submitted a Marketing Authorization ...

Thirty patients have received the gene therapy within a clinical trial and early-access program, and the foundation also hopes to seek approval in the US.

Telethon Foundation is seeking approval for a gene therapy to treat the rare disease Wiskott-Aldrich syndrome.