Veterans fighting the muscle disease known as IBM say they want the U.S. government to recognize their condition as ...
Flesh turning to stone sounds like something from fantasy, but this rare genetic disease does something similar, often doing ...
Ultragenyx’s Rare Bootcamp gives families a roadmap to help drive research and develop new treatments for rare diseases.
Lozano is a rare disease mom, neuroscience Ph.D. candidate at UC Davis, and board member for the PURA Syndrome Foundation. In May, a historic moment in science and medicine was captured in a single ...
Thousands of times per year, a family’s moment of joy turns to unexpected grief. A seemingly healthy infant stops smiling or ...
Key market opportunities include increased diagnosis of multicentric Castleman disease, precision immunotherapy, and expansion of specialty clinics. Growth is driven by targeted IL-6 therapies, rising ...
Mississippi is launching a Rare Disease Task Force within the Mississippi Rare Disease Advisory Council to study issues ...
Families and researchers are advocating for Huntington's disease to be recognized as a rare disease in India to establish a ...
Across America, millions of parents of children with rare diseases are in a race against time, hoping that new treatments will be developed fast enough to save their kids. Thanks to advances in ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results