The field of gene editing recently got a major boost from Massachusetts-based Beam Therapeutics, and the company’s Durham ...

2024 — Using state-of-the-art technology, researchers have identified several specific steps needed for CRISPR to become active and perform its gene editing ... Single-Dose Gene Therapy Is ...

AccurEdit Therapeutics today announced that its innovative in vivo gene editing product, ART001, has obtained Orphan Drug Designation (ODD) from the U.S. Food and Drug Administration (FDA).

The first-of-its-kind facility in India has received an investment of $75 million from the company to build it vertically ...

In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form ...

Genetic testing is transforming depression treatment by tailoring antidepressants to your DNA for better results and fewer ...

Betsy Arakawa, the classical pianist married to Gene Hackman, died last month of hantavirus pulmonary syndrome, a rare infectious disease linked to rodents, New Mexico authorities announced Friday.

The University of Bristol research team used animal models to compare patient responses to AAV therapy, studying male and female eye cells across different age groups (young, middle-aged and older ...

Many biological scientists and clinicians have developed and innovated a variety of emerging therapeutic tools and strategies for different diseases such as gene therapy. This therapy modifying genes ...

Together, the manufacturer and the nonprofit are developing a gene therapy treatment that could change the lives of children with conditions that currently have no cure. Childs Cure co-founders ...

A one-time injection of a novel gene therapy was able to save mice and a newborn calf from succumbing to maple syrup urine disease (MSUD), suggesting the approach could one day be used to treat ...