The future of medicine is being shaped by a confluence of factors at play. If there are worries galore around drug resistant ...
Steward Partners Investment Advisory LLC acquired a new stake in BioLife Solutions, Inc. (NASDAQ:BLFS – Free Report) in the ...
Gene therapy pioneer Jim Wilson and researcher Kiran Musunuru are using contrasting approaches to overcome “irrational ...
Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...
In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form ...
Indian vaccine maker Bharat Biotech said on Thursday it had invested $75 million in its first cell and gene therapy (CGT) facility in the southern Indian state of Telangana and expects its new ...
By replacing the defective gene associated with Dravet syndrome in mice, scientists successfully alleviated symptoms without ...
To Novartis, fresh late-stage data support the idea that its intrathecal drug, which has the same active ingredient as Zolgensma, could be approved for a broad range of spinal muscular atrophy ...
In a groundbreaking advancement for families grappling with the challenges of Dravet syndrome, a rare and life-altering form ...
A pair of privately-held developers of editing-based therapies have some successes to show for their recent efforts to ...
In the time since the Novartis gene therapy Zolgensma was approved for babies with spinal muscular atrophy, other treatments ...
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