Art and science are disciplines that have historically co-existed as polarised entities. However, artists and scientists both ...

Jonathan James, CEO, Hope Charities, discusses the critical importance of maintaining access to life-saving medications for ...

Fostering dialogue between neurologists, researchers, patient representatives, and policymakers is an important step towards ...

The show is based on the real story of Natalia Grace, a Ukrainian girl born with spondyloepiphyseal dysplasia congenita.

After being used since the 1940s in various industries, asbestos is now linked to severe health risks, including asbestosis, ...

INmune Bio's high-upside potential with CORDStrom for RDEB and XPro for Alzheimer's, offering up to 144.8x returns. Click ...

Health Canada has granted approval for Biogen’s Skyclarys (omaveloxolone) to treat Friedreich’s ataxia (FA), a rare, ...

Evaluate, the leading provider of market insights for the pharmaceutical industry, today released its 2025 Orphan Drug Report highlighting forecasts for the orphan drug market out to 2030. The 2025 ...

AstraZeneca acquired the hypoparathyroidism therapy eneboparatide as part of a buyout of Amolyt Pharma in July 2024.

Batoclimab is an anti-FcRn treatment being developed for a range of autoimmune diseases and active thyroid eye disease (TED).

Bexobrutideg, a bioavailable agent, was granted orphan drug designation by the FDA for Waldenström macroglobulinemia, a type ...

BioArctic AB (publ) (Nasdaq Stockholm: BIOA B) announced today that the US FDA Office of Orphan Products Development (OOPD) has granted orphan drug ...