A new federal grant is allowing Moffitt Cancer Center to study a rare and aggressive disease that affects cancer patients, ...
Bella Hadid has spent a month at St. George Hospital near Munich undergoing intensive treatment for chronic Lyme disease.
The FDA has approved Jascayd (nerandomilast) tablets to treat idiopathic pulmonary fibrosis, a rare, progressive lung disease that can cause scarring ...
In the journal Childhood in the Past, Ph.D. candidate Duru Yağmur Başaran published the results of an analysis of an over 900 ...
UCB's experimental medicine for rare disease thymidine kinase 2 deficiency (TK2d) has been shown to reduce the risk of death ...
Working with agency partner DCX Growth Accelerator, GeneDX takes direct aim at the issue of underdiagnosis of pediatric rare diseases.
The US Food and Drug Administration (FDA) has selected Abeona Therapeutics’ ABO-503 gene therapy for X-linked retinoschisis ...
Cade was diagnosed with a rare, neurodegenerative disease when he was 2½. Now 4, Cade has been receiving treatment for the ...
Since the 1960s, Texas has screened newborns for a variety of rare diseases — like sickle cell anemia and cystic fibrosis.
In a closely watched case, Roche suffered a setback as a court said it would permit a generic version of its rare disease ...
For Ms Miria Mukiibi Kibirige, that struggle is a daily reality. She cares for two children living with epidermolysis bullosa ...