US regulators laid out new guidelines for approving custom-made treatments for individual patients, a move that could bring ...
Seles’ first symptoms appeared suddenly around three years ago. She began having double vision and weakness in her arms and ...
Myelin oligodendrocyte glycoprotein antibody-associated disease (MOGAD) is a rare autoimmune condition in which the body's ...
Around 25 million Americans have a rare genetic disease, and many of them struggle with not only a lack of effective ...
In FSGS, podocytes are damaged, like a net with torn holes, allowing protein to leak into the urine, creating a harmful ...
SEPANG: Malaysia will lead efforts for a South-East Asia Declaration and Action Plan on Rare Diseases to improve diagnosis, ...
Delhi High Court has constituted a panel of experts to oversee a crowdfunding platform for rare diseases, aiming to boost ...
The complex molecular underpinnings of genetic and rare diseases offer a promising avenue for scientific exploration and ...
Tenaya Therapeutics said on Friday the U.S. Food and Drug Administration has placed a clinical hold on its trial of an ...
We have a heartwarming update about a story we brought you just a few weeks ago! Brighton is a three-year-old girl with a rare mitochondrial disease and she is about to step into a whole new way of ...
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