Michigan Resident Dies From Donated Kidney Tainted With Rabies
WTOL, a media outlet based in Toledo, Ohio, first reported on the unusual death Wednesday, which was confirmed by health ...
After a Rare Diagnosis, This Man Found Strength in Fitness. Now, His Story Is Inspiring Others
A neuromuscular disease put Anthony Monaco in a wheelchair. But it hasn't stopped him from competing in CrossFit.
JD Supra3h
FDA Publishes Case Studies and User Guide for Rare Disease Drug Developers
Drug development programs face unique challenges in demonstrating the safety and effectiveness of drugs for treating rare diseases. The ...
Japan Approves BridgeBio Pharma-AstraZeneca Partnered Rare Heart Disease Drug
Based on the terms of the agreement, BridgeBio will receive a $30 million milestone payment upon approval in Japan, as well ...
Freddie Freeman's wife shares vital health update on son, 4, amid battle with heartbreaking rare disease
The start of another season of Major League Baseball isn't the only piece of good news in the Freeman household.
Healio5h
FDA recap: First new treatment for stroke in 3 decades, generic rivaroxaban and more
The FDA recently approved the first treatment in nearly 30 years for acute stroke, and the agency also approved a novel drug ...
Regulus Therapeutics Stock Shoots Higher After Positive Results From Investigational Drug For Rare Type Of Kidney Disease
Regulus Therapeutics' Phase 1b study shows farabursen 300 mg slowed kidney volume growth in ADPKD patients with a favorable ...
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Kansas nonprofit gains new partnership to help families battling rare diseases
Coming Together for a Cure partnered with Cariloop to give families free access to its caregiver support platform.
Soleno Therapeutics execs reap stock windfall after FDA approves rare disease drug
Soleno Therapeutics' FDA-approved drug for Prader Willi Syndrome triggers executive stock bonuses as the company's value ...
Rutgers University8h
Four Rutgers Researchers Named Fellows of the American Association for the Advancement of Science
Rutgers faculty elected to the newest class of fellows of the American Association for the Advancement of Science (AAAS) are ...
L.J. Smith, author of ‘Vampire Diaries' novels, dead at 66
L.J. Smith, the author of the Vampire Diaries novels as well as dozens of other young-adult fiction books, has died at the ...
Soleno jumps as analysts say US nod for rare disease drug transforms treatment options
Shares of Soleno Therapeutics jumped nearly 40% in premarket hours on Thursday, after the company's drug for a rare metabolic condition became the first such treatment to receive U.S. regulatory nod.