Intellia Therapeutics CEO John Leonard explained the circumstances of the patient death at the J.P. Morgan Healthcare ...

Speaking at the Asian Thalassemia Conclave 2026 held at Kamala Hospital, the Minister called for a ‘collective social movement’ to eradicate the genetic blood disorder ...

Victoria Gray spent 34 years battling the debilitating pain of sickle cell disease. Then she volunteered to be the world's first "prototype" for a CRISPR therapy, based on technology invented at UC ...

Jesy Nelson has broken down in tears as she discussed her eight-month-old twin babies’ diagnosis that might result in them ...

From immune cell therapies to measles outbreaks to federal attacks on public health, these are some of the health topics we’ll be watching next year ...

INDIANAPOLIS (WISH) — For the first time, scientists say new therapies have the power to cure sickle cell disease. The disease is a devastating, inherited blood disorder that affects an estimated ...

ORLANDO, Fla. — Recurrent pain episodes are the leading reason for emergency department (ED) visits among patients with sickle cell disease, but adherence to established acute pain management ...

Adam Feuerstein is a senior writer and biotech columnist, reporting on the crossroads of drug development, business, Wall Street, and biotechnology. He is also a co-host of the weekly biotech podcast ...

Please provide your email address to receive an email when new articles are posted on . Ninety percent of patients with sickle cell disease survived at least 7 years after allogeneic HCT. A majority ...

Preliminary results from two trials of the gene therapy exagamglogene autotemcel (exa-cel) suggest the therapy offers an effective cure for beta-thalassemia and sickle cell disease in children younger ...

Makenzie’s first sickle cell pain crisis came without warning. She was scared and felt alone. Not only was the pain excruciating, but her parents weren’t there—her two worst fears at once. She spent ...

Chicago’s South Side residents now have access to a new sickle-cell treatment clinic at Roseland Community Hospital. On Monday, Roseland held a ribbon-cutting ceremony introducing Dr. Mahoud Mahafzah ...