Standard genetic sequencing approaches can tell you a lot about the genetic makeup and activity in a sample, like a piece of ...

Can we take genetic "pills" for disease-related mutations? No, not yet, but our knowledge of the human genome sequence has enabled the development of other gene-based therapeutic approaches.

View Full Profile. Learn about our Editorial Policies. Genetic medicines could treat certain diseases, however, the current delivery systems available—viral vectors and lipid nanoparticles (LNPs)—pose ...

However, because conventional LNPs are primarily taken up by the liver, genetic medicines are hindered in their ability to treat a wealth of diseases that already have validated biological targets.

Flagship Pioneering's latest biotech launch, Mirai Bio, aims to help genetic medicine developers find the best way to get their drugs to patients. The new Cambridge, Massachusetts-based company ...