Opioid orphans: Grandparents struggle to raise children left behind
Between 2011 to 2021, an estimated 321,566 children lost a parent to drug overdose. Parental deaths from drug overdose rose ...
Korro Bio gets Orphan Drug Designation from FDA for its genetic disorder treatment
Korro Bio received U.S. FDA's orphan drug designation for investigational medicine KRRO-110 to treat Alpha-1 Antitrypsin ...
Korro Bio's KRRO-110 Gets FDA Orphan Drug Designation
Korro Bio disclosed that the Food and Drug Administration granted orphan drug designation to its potential genetic disorder drug KRRO-110. Shares rose 17.6% to $29 in premarket trading. The stock is ...
KRRO-110 Receives Orphan Drug Designation from U.S. FDA for Alpha-1 Antitrypsin Deficiency
KRRO-110 is the first RNA editing development candidate from Korro’s proprietary OPERA TM platform and is currently being evaluated in the Phase 1/2a REWRITE clinical study for AATD. Dosing of the ...
Korro Bio receives ODD from U.S. FDA for AATD
Korro Bio (KRRO) announced that the U.S. Food and Drug Administration has granted orphan drug designation, ODD, to the investigational medicine ...
Plus Therapeutics soars on FDA Orphan Drug Designation for lung cancer treatment
Plus Therapeutics (NASDAQ:PSTV) shares rose 71% after the company said on Thursday that the U.S. FDA has granted Orphan Drug ...
pharmaphorum14d
Rare diseases, orphan drugs and parent companies
Continuing our rare disease theme, Catherine McLoughlin shares her thoughts on the orphan drug market and how pharma / biotech companies may change their focus to rare diseases in the future.
PharmiWeb16d
Orphan Drugs Market Poised for Remarkable Growth: Expected to Expand US$ 424.0 Bn by 2034 - TMR Analysis
Orphan drugs are essential in addressing rare diseases, which, despite affecting a small percentage of the population, demand innovative medical solutions. These drugs are primarily used to treat ...
London South East17d
Positive EMA Opinion on Orphan Drug Designation
issued positive opinion on Orphan Drug Designation (ODD) for bexmarilimab - Positive opinion on Orphan Drug Designation further strengthens bexmarilimab program by offering clinical development ...
Access WDUN17d
Former CDC official from Gainesville dies at age 69
Hodge authored more than 100 peer-reviewed publications, book chapters, patents, IND and Orphan Drug applications during his career. In addition, he spent six years in an NIH study group. At the ...
verywellhealth21d
List of Approved HIV Antiretroviral Drugs
Antiretroviral drugs are used to treat HIV infection. They work by blocking a stage of the virus's life cycle and, by doing so, prevent the virus from replicating. The drugs are organized into six ...
Cfr.org23d
Mexico’s Long War: Drugs, Crime, and the Cartels
Subscribe to the Daily News Brief. Mexican authorities have been waging a deadly battle against drug cartels for nearly two decades, but with limited success. Thousands of Mexicans—including ...