BARCELONA, Spain I March 13, 2025 I SpliceBio, a clinical-stage genetic medicines company pioneering Protein Splicing to address diseases caused by mutations ...

The latest HPRA inspection in February 2025 was highly successful-both QC licences were renewed, and viral vector manufacturing was added to the MIA (IMP) licence. This means the Shannon site can ...

The FDA has granted orphan drug designation (ODD) to rhenium (186Re) obisbemeda for the potential treatment of patients with leptomeningeal metastases (LM) in patients with lung cancer. Rhenium ...

EN001, a novel therapy under development by ENCell, has been granted Orphan Drug Designation by the U.S. FDA for the treatment of Charcot-Marie-Tooth (CMT) disease. Phase 1 clinical trial ...

The global orphan drug market size was USD 154.20 Billion in 2022 and is expected to register a rapid revenue CAGR of 12.3 % during the forecast period. The global orphan drug market is witnessing ...

A disease is classed as rare when it affects fewer than one in 2,000 people. New orphan drugs can provide rare disease patients with hope for a better quality of life when all existing treatment ...

The European orphan drug market is growing and is already comparable in size and scope to the US market. The European Union (EU) counts 36 million rare disease patients, and the European market is ...

The Police Command in Lagos State has clarified that the man seen in a viral video being manhandled by police officers was arrested for alleged illegal possession of drugs, not for wearing ...

Ludhiana: Soon after the video of an argument between a woman, allegedly a drug peddler, and the sarpanch of Narangwal village went viral, Ludhiana rural police got her "illegal" property ...