The Senate Parliamentarian reversed course on a small provision in the One Big Beautiful Bill Act that could boost cures for ...

For payers, claims for rare disease treatments used to be uncommon. Not anymore, thanks to an increasing number of new, ...

Syntis Bio, Inc. (Syntis), a clinical-stage biopharmaceutical company revolutionizing oral therapies for obesity, diabetes ...

Kolkata: Prodded by the Calcutta HC, the state on Tuesday submitted that a 50-bed critical care unit at the Kolkata Police ...

June is Alzheimer's and Brain Awareness Month. Colbie Schueneman, 6, is sharing her story with KIF1A, also known as KAND.

For Bethany Duckworth, being an active mom wasn’t just a dream, it was her plan. "It's depressing," Duckworth said. "It's sad ...

Jack Troyano mostly lives like a typical boy. But the frequent shots and weekly infusions he gets for juvenile arthritis tell ...

Apellis and Sobi have amended their partnership agreement for paroxysmal nocturnal hemoglobinuria (PNH) treatment Empaveli, ...

Tel Aviv University researchers say their investigation into a GRIN2D gene mutation will advance research into a protein ...

Three major Mount Sinai research studies offer new hope for patients facing chronic lymphocytic leukemia (CLL), a rare type ...

The pivotal trial for Neurogene's Rett syndrome gene therapy makes use of baseline controls and a rigorous endpoint that ...