Country music icon retiring with rare disease. Here’s what to know
He took the stage and was great last week at the Grand Ole Opry’s 100th anniversary show, and now he is down to just two ...
Meet Daniela, the 12-year-old girl battling a rare disease who’s become the UConn women’s secret weapon
When the UConn women’s basketball team takes the court, they know that no matter what happens, they’ve got the support of one ...
Dallas scientists granted $420K to test gene therapy for rare neurological disease
Childhood-onset striatonigral degeneration is a rare genetic disorder that robs children of the ability to walk and speak by ...
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Soleno Therapeutics’ ‘life-changing’ rare-disease drug approved
The FDA Wednesday approved the first drug to treat people with Prader-Willi syndrome, a rare genetic disease that causes an ...
ScienceAlert on MSN1d
Drug For Rare Disease Turns Human Blood Into Mosquito Poison
Scientists have a radical new plan for controlling mosquito numbers and fighting malaria: lacing human blood with a drug that ...
Rare disease drug nitisinone makes human blood deadly to mosquitoes
A study in Science Translational Medicine found when patients take the drug nitisinone, their blood becomes deadly to ...
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Kansas nonprofit gains new partnership to help families battling rare diseases
Coming Together for a Cure partnered with Cariloop to give families free access to its caregiver support platform.
Soleno jumps as analysts say US nod for rare disease drug transforms treatment options
Shares of Soleno Therapeutics jumped nearly 40% in premarket hours on Thursday, after the company's drug for a rare metabolic condition became the first such treatment to receive U.S. regulatory nod.
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Cherokee Nation Rare Disease Task Force outlines recommendations tribe can take to assist those with rare diseases
The Cherokee Nation Health Services Rare Disease Task Force has released a report outlining progress made over the past year ...
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Availability Of Drug For Rare Diseases At Economical Prices Material Factor To Be Considered Before Restraining Via Interim Injunction: Delhi HC
The Delhi High Court has observed that availability of a drug for treatment of rare diseases at economical and competitive ...
For kids with extremely rare diseases, this promising technology provides a lifeline | Opinion
Genetically targeted technologies are built on Nobel Prize-winning science. They represent a scientific “quantum leap” that ...
LJ Smith dead: The Vampire Diaries author who inspired TV show dies after battle with rare disease
Author LJ Smith, who was behind the Vampire Diaries series that inspired the hit TV show of the same name, has died at the ...