US FDA Approves First Treatment for Rare Genetic Disorder Prader-Willi Syndrome
(Reuters) -The U.S. Food and Drug Administration on Wednesday approved Soleno Therapeutics' drug to treat a rare genetic ...
US FDA greenlights first-ever treatment for rare genetic disorder
The U.S. Food and Drug Administration approved Soleno Therapeutics' drug to treat a rare genetic disorder on Wednesday, ...
Her son has a rare genetic disorder, so this Connecticut mom is taking fight for funding to D.C.
Families in Connecticut and beyond are looking for answers when it comes to treating Angelman Syndrome, but fear funding ...
Dallas scientists granted $420K to test gene therapy for rare neurological disease
Childhood-onset striatonigral neurodegeneration robs children of the ability to walk and talk by age five. Researchers at ...
Rare loss-of-function variants in HECTD2 and AKAP11 confer risk of bipolar disorder
Scientists at deCODE genetics/Amgen have identified associations between bipolar disorder and rare loss-of-function variants ...
deCODE genetics: Rare loss-of-function variants in HECTD2 and AKAP11 confer a risk of bipolar disorder
Scientists at deCODE genetics, a subsidiary of Amgen, reveal today in Nature Genetics associations between rare ...
Soleno Therapeutics execs reap stock windfall after FDA approves rare disease drug
Soleno Therapeutics' FDA-approved drug for Prader Willi Syndrome triggers executive stock bonuses as the company's value ...
Her Baby Had to Be Revived 8 Times in the NICU. Now She's Talking About His Rare Condition to Help Moms Like Her (Exclusive)
Audrey Kandil tells PEOPLE her son, Rami, was born with cerebrocostomandibular syndrome, which is a rare genetic disorder ...
Ontario Brain Institute partners with EpiSign to advance diagnosis of rare genetic disorders
The Ontario Brain Institute (OBI) is pleased to announce a joint new initiative with EpiSign Inc., paving the way for improved diagnosis and care for people with rare neurological genetic disorders.
News Medical on MSN1d
Scientists uncover rare gene variants that help people live past 100
Researchers studying over 2,000 Ashkenazi Jewish centenarians uncovered two rare IGF-1 gene variants linked to exceptional ...
Rolling Out1d
Promising drug cuts Alzheimer’s risk by half in rare cases
Research shows experimental anti-amyloid drug reduced cognitive symptom risk by 50% in people with rare genetic mutations ...
STAT1d
Soleno Therapeutics’ ‘life-changing’ rare-disease drug approved
The FDA Wednesday approved the first drug to treat people with Prader-Willi syndrome, a rare genetic disease that causes an ...