Rare diseases are not actually that rare. Collectively they affect 500 million people around the world. Some, such as Huntington’s disease and sickle cell disease, affect many thousands, others only ...

Stargardt programs address ABCA4 payload constraints via dual-AAV platforms (VG801, AAVB-039) and explore first ...

Watch Toronto hospital looks to provide life-long care to sickle cell disease patients closer to home Video Online, on GlobalNews.ca ...

As Uganda rolls out mandatory nationwide screening of newborns for sickle cell disease this month, a gene therapy celebrated in the United States and Europe remains financially out of reach for most ...

Rapper Lil Poppa, 25, has died, with unverified suicide reports circulating. His death raises concerns due to his battle with sickle cell anemia, which he previously discussed. The cause of death ...

CRISPR Therapeutics (NASDAQ:CRSP) executives highlighted progress across its oncology and autoimmune cell therapy pipeline during Citi’s Virtual Oncology Leadership Summit, emphasizing updates on its ...

Florida rapper Lil Poppa has died at 25. Fans are remembering him while talking openly about his battle with sickle cell ...

Steffen Schmitz-Valckenberg, MD, is professor of ophthalmology and visual science and the Jon M. Huntsman Presidential Chair at John A. Moran Eye Center at the University of Utah in Salt Lake City, UT ...

Chlamydia pneumoniae is an intracellular bacterium that commonly causes respiratory infections such as pneumonia and sinusitis. It can persist in the body by evading immune defenses, leading to ...

Tesla Inc. isn’t waiting around to see if Elon Musk’s 100-gigawatt solar ambition is feasible — it’s already acting on it. The company is evaluating multiple sites across the US to begin manufacturing ...

B.J. Mathews loves basketball and is dealing with sickle cell disease. That brought him into the orbit of the Golden Eagles.

The electric vehicle giant has started turning Elon Musk's 100-gigawatt solar goal into an active U.S. manufacturing push by scouting multiple sites to make solar cells. The company is weighing an ...