Thanks to a groundbreaking genetic treatment, Sebastien Beauzile is the first person in New York to be cured of the disease.

A recent Vanderbilt study has found a cure for sickle cell disease, a blood disorder where the body creates mutated red blood ...

This episode highlights how Watson's medical format can address real-world issues in dramatically interesting ways, with a ...

A new study published in Cell Reports reveals a breakthrough discovery linking genetic variants in the gene ITSN1 to a significantly elevated risk of Parkinson's disease, a neurodegenerative condition ...

Vertex Pharmaceuticals operates in a profitable subsector and is poised for further success, says Dr Michael Tubbs ...

Over the last few months, there have been multiple reports on new treatments for sickle cell disease. In this feature, we highlight the biggest updates in this field and think about what the future ...

7 Other relevant clinical information, such as the patient’s sickle cell genotype, frequency of painful crises, typical number of days of hospitalizataion during crises, blood cell counts, and medical ...

It is well-established that patients with sickle cell disease (SCD) are at substantial risk of neurological complications, including overt and silent stroke, microstructural injury, and cognitive ...

The current study suggests P63+ progenitor cell therapy is safe in patients with ILD. The authors attribute this to acquisition of cells from a healthy upper lobe site, removed from the lung fibrosis.

Some types of blood clotting disorders may cause excessive formation ... Routine blood tests, such as a complete blood count (CBC), can detect anemia (low red blood cell count or function) or low ...

The authors provide convincing evidence that P63+ progenitor cell therapy can be safely delivered in patients with ILD. However, given that this is a Phase 1 study, conclusions regarding efficacy ...

but children with sickle cell disease receive these immunizations in infancy or early childhood. Two vaccines are required. The first is called Menveo or Menquadfi, and it protects against ...